Clinical Trials Directory

Trials / Completed

CompletedNCT01640717

A Retrospective, Observational, Noninterventional Data Collection Study for Patients With Molybdenum Cofactor Deficiency Who Have Been Previously Treated With Cyclic Pyranopterin Monophosphate (cPMP)

Status
Completed
Phase
Study type
Observational
Enrollment
15 (actual)
Sponsor
Origin Biosciences · Industry
Sex
All
Age
1 Day
Healthy volunteers
Not accepted

Summary

The primary objective is to assess safety and efficacy data of Escherichia coli-derived cPMP in patients with molybdenum cofactor deficiency (MoCD).

Conditions

Timeline

Start date
2012-11-01
Primary completion
2014-10-01
Completion
2014-10-01
First posted
2012-07-16
Last updated
2019-03-19

Locations

13 sites across 6 countries: United States, Australia, Germany, Netherlands, Turkey (Türkiye), United Kingdom

Source: ClinicalTrials.gov record NCT01640717. Inclusion in this directory is not an endorsement.