Trials / Sponsors / Origin Biosciences
Origin Biosciences
Industry · 5 registered clinical trials.
| Status | Trial | Phase | Started |
|---|---|---|---|
| Completed | Study of ORGN001 (Formerly ALXN1101) in Neonates, Infants and Children With Molybdenum Cofactor Deficiency (MO Molybdenum Cofactor Deficiency, Type A | Phase 2 / Phase 3 | 2016-05-01 |
| Completed | Safety & Efficacy Study of ORGN001 (Formerly ALXN1101) in Pediatric Patients With MoCD Type A Currently Treate Molybdenum Cofactor Deficiency, Type A | Phase 2 | 2014-04-01 |
| Completed | A Natural History Study of Molybdenum Cofactor and Isolated Sulfite Oxidase Deficiencies Molybdenum Cofactor Deficiency, Isolated Sulfite Oxidase Deficiency | — | 2013-08-01 |
| Completed | Phase 1 Single Dose Study of ALXN1101 in Healthy Volunteers Molybdenum Cofactor Deficiency (MoCD), Rare Autosomal Recessive Disorder, Deficiency of Activity of Molybdenum-dependent Enzymes (Sulfite Oxidase [SOX], Xanthine Dehydrogenase, and Aldehyde Oxidase) | Phase 1 | 2013-06-01 |
| Completed | A Retrospective, Observational, Noninterventional Data Collection Study for Patients With Molybdenum Cofactor Molybdenum Cofactor Deficiency | — | 2012-11-01 |