Wolman Disease

13 registered clinical trials studyying Wolman Disease — 4 currently recruiting.

Status	Trial	Sponsor	Phase
Recruiting	The Effect of Kegel Exercise and Ba Duan Jin Applications on Premenopausal Women With Urinary Incontinence NCT06287658	Ondokuz Mayıs University	N/A
Recruiting	Registry of Patients Diagnosed With Lysosomal Storage Diseases NCT05619900	University of California, San Francisco	—
Recruiting	PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders) NCT04532047	University of California, San Francisco	Phase 1
Unknown	Prevalence and Risk Factors of Women Mental Health Disorders NCT04792671	Assiut University	—
Completed	Breakfast for Young Women NCT04652713	University of Aarhus	N/A
Recruiting	Lysosomal Acid Lipase (LAL) Deficiency Registry NCT01633489	Alexion Pharmaceuticals, Inc.	—
Completed	Human Placental-Derived Stem Cell Transplantation NCT01586455	New York Medical College	Phase 1
Completed	Safety, Tolerability, Efficacy, Pharmacokinetics, and Pharmacodynamics of Sebelipase Alfa in Children With Gro NCT01371825	Alexion Pharmaceuticals, Inc.	Phase 2 / Phase 3
Completed	A Retrospective Natural History Study of Patients With Lysosomal Acid Lipase Deficiency/Wolman Phenotype NCT01358370	Alexion Pharmaceuticals, Inc.	—
Completed	Wolman/CESD Natural History Chart Review and Longitudinal Follow-Up NCT01884220	Children's Hospital Medical Center, Cincinnati	—
Completed	HSCT for High Risk Inherited Inborn Errors NCT00383448	Masonic Cancer Center, University of Minnesota	Phase 2
Unknown	Study of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoie NCT00005900	Fairview University Medical Center	—
Completed	Stem Cell Transplant for Inborn Errors of Metabolism NCT00176904	Masonic Cancer Center, University of Minnesota	Phase 2 / Phase 3