Trials / Conditions / Sphingomyelin Lipidosis
Sphingomyelin Lipidosis
5 registered clinical trials studyying Sphingomyelin Lipidosis.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Completed | A Prospective and Retrospective Cohort Study in Patients With Chronic Forms of Acid Sphingomyelinase Deficienc NCT04106544 | Sanofi | N/A |
| Completed | Efficacy, Safety, Pharmacodynamic, and Pharmacokinetics Study of Olipudase Alfa in Patients With Acid Sphingom NCT02004691 | Genzyme, a Sanofi Company | Phase 2 / Phase 3 |
| Completed | Safety, Tolerability, PK, and Efficacy Evaluation of Repeat Ascending Doses of Olipudase Alfa in Pediatric Pat NCT02292654 | Genzyme, a Sanofi Company | Phase 1 / Phase 2 |
| Completed | A Long-Term Study of Olipudase Alfa in Patients With Acid Sphingomyelinase Deficiency NCT02004704 | Genzyme, a Sanofi Company | Phase 2 |
| Approved For Marketing | Compassionate Use Program for Olipudase Alfa Enzyme Replacement Therapy for Patients With Chronic Acid Sphingo NCT04877132 | Sanofi | — |