Trials / Conditions / Sphingolipidoses
Sphingolipidoses
6 registered clinical trials studyying Sphingolipidoses — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Recruiting | SPL Insufficiency Syndrome (SPLIS)/NPHS14: a SPLIS Observational Study and Patient Registry (International) NCT04885179 | University of California, San Francisco | — |
| Completed | Lyso-Gb1 as a Long-term Prognostic Biomarker in Gaucher Disease NCT02416661 | CENTOGENE GmbH Rostock | — |
| Terminated | Natural History Study of Children With Metachromatic Leukodystrophy NCT01963650 | Shire | — |
| Active Not Recruiting | MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis NCT02171104 | Masonic Cancer Center, University of Minnesota | Phase 2 |
| Completed | Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders NCT01043640 | Masonic Cancer Center, University of Minnesota | Phase 2 |
| Terminated | Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism NCT00668564 | Masonic Cancer Center, University of Minnesota | Phase 2 |