Trials / Conditions / Severe Combined Immunodeficiency Due to ADA Deficiency
Severe Combined Immunodeficiency Due to ADA Deficiency
5 registered clinical trials studyying Severe Combined Immunodeficiency Due to ADA Deficiency.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Unknown | Methodology Study of Retroviral Insertion Site Analysis in Strimvelis Gene Therapy NCT04959890 | Fondazione Telethon | — |
| Withdrawn | A Clinical Study to Enable Process Validation of Commercial Grade OTL-101 NCT04140539 | University of California, Los Angeles | Phase 2 / Phase 3 |
| Completed | Evaluating the Effectiveness of STRIMVELIS Risk Minimization Measures (RMMs) NCT03232203 | Fondazione Telethon | — |
| Completed | Efficacy and Safety of the Cryopreserved Formulation of OTL-101 in Subjects With ADA-SCID NCT03765632 | Great Ormond Street Hospital for Children NHS Foundation Trust | Phase 1 / Phase 2 |
| Completed | Efficacy and Safety of the Cryopreserved Formulation of OTL-101 in Subjects With ADA-SCID NCT02999984 | University of California, Los Angeles | Phase 1 / Phase 2 |