Trials / Conditions / Sanfilippo Syndrome Type A
Sanfilippo Syndrome Type A
3 registered clinical trials studyying Sanfilippo Syndrome Type A — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Recruiting | Phase 1 Study of GC1130A in Patients With Sanfilippo Syndrome Type A (MPS IIIA) NCT06567769 | GC Biopharma Corp | Phase 1 |
| Completed | Neurobehavioral Phenotypes in MPS III NCT01873911 | University of Minnesota | — |
| Completed | A Study of Patients With Sanfilippo Syndrome Type A (MPS IIIA) NCT01047306 | Shire | — |