Clinical Trials Directory

Trials / Conditions / Niemann-Pick Diseases

Niemann-Pick Diseases

6 registered clinical trials studyying Niemann-Pick Diseases2 currently recruiting.

StatusTrialSponsorPhase
RecruitingA Real-world Long-term Safety and Immunogenicity Study of Olipudase Alfa Therapy in Pediatric Patients Less Th
NCT06192576
Sanofi
CompletedPREDIGA 2: Spanish Acronym of "Educational and Diagnostic Project for Gaucher and ASMD"
NCT05641103
Fundación Española de Hematología y Hemoterapía
CompletedHealth Insurance Literacy and Challenges in Accessing Health Services in Niemann-Pick
NCT04469894
National Niemann-Pick Disease Foundation
CompletedInduced Pluripotent Stem Cells for Niemann Pick Disease
NCT03883750
CENTOGENE GmbH Rostock
RecruitingLongitudinal Study of Neurodegenerative Disorders
NCT03333200
University of Pittsburgh
CompletedSaccadic Eye Movements in Patients With Niemann-Pick Type C Disease
NCT00316498
National Eye Institute (NEI)Phase 1