Clinical Trials Directory

Trials / Conditions / Mucopolysaccharidosis Type II

Mucopolysaccharidosis Type II

7 registered clinical trials studyying Mucopolysaccharidosis Type II — 1 currently recruiting.

StatusTrialSponsorPhase
CompletedA Study of the Tolerance, Safety, and Pharmacokinetics of GNR-055 in Healthy Volunteers
NCT06475404
AO GENERIUMPhase 1
RecruitingA Multi-cohort Study of Safety, Efficacy, PK and PD of GNR-055 in Patients With Mucopolysaccharidosis Type II
NCT05208281
AO GENERIUMPhase 2 / Phase 3
CompletedCore Outcome Set for Head, Neck and Respiratory Disease in Mucopolysaccharidosis II
NCT06022380
Manchester University NHS Foundation Trust—
CompletedA Multi-cohort Study of the Tolerance, Safety, and Pharmacokinetics of GNR-055 in Healthy Volunteers
NCT04539340
AO GENERIUMPhase 1
CompletedParental Coping With Challenging Behavior in Mucopolysaccharidosis Type I-III
NCT03161171
University Hospital Heidelberg—
CompletedEffects of Adalimumab in Mucopolysaccharidosis Types I, II and VI
NCT02437253
Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical CenterPhase 1 / Phase 2
CompletedLongitudinal Studies of Brain Structure and Function in MPS Disorders
NCT01870375
University of Minnesota—