Clinical Trials Directory

Trials / Conditions / Mucopolysaccharidoses

Mucopolysaccharidoses

14 registered clinical trials studyying Mucopolysaccharidoses2 currently recruiting.

StatusTrialSponsorPhase
Not Yet RecruitingPediatric Arthropathy Beyond Inflammation: Clinical Spectrum and Diagnostic Approach at Assiut University Chil
NCT07173010
Assiut University
UnknownValidation and Reliability of Iris Cameras in Mucopolysaccharidoses
NCT05354219
Manchester University NHS Foundation Trust
Active Not RecruitingCardiovascular Structure and Function in the Mucopolysaccharidoses
NCT05063435
Children's Hospital of Orange County
UnknownEvaluation of Cardiac Affections in Patients With Mucopolysaccharidosis (MPS) in Assuit University Children Ho
NCT04637646
Assiut University
CompletedRespiratory Cathepsins, Proteases Inhibitors and Glycosaminoglycans (GAG) in Mucopolysaccharidosis
NCT04112602
University Hospital, Tours
CompletedAssessment of Factors That Affected Respiratory Parameters in Mucopolysaccharidoses Patients
NCT04491747
Hacettepe University
UnknownEvaluation of Losartan on Cardiovascular Disease in Patients With Mucopolysaccharidoses IV A and VI
NCT03632213
Hospital de Clinicas de Porto AlegrePhase 2
UnknownA Cross-specialty Collaboration Platform for Mucopolysaccharidosis Confirmative Diagnosis
NCT03017677
Mackay Memorial Hospital
CompletedLeukoSEQ: Whole Genome Sequencing as a First-Line Diagnostic Tool for Leukodystrophies
NCT02699190
Children's Hospital of Philadelphia
RecruitingThe Myelin Disorders Biorepository Project
NCT03047369
Children's Hospital of Philadelphia
UnknownNew Imaging Technology to Assess Effect of Enzyme Replacment Therapy on Eye Disease Progession in Mucopolysacc
NCT02583152
Manchester Royal Eye Hospital
CompletedCarotid Structure and Function in MPS Syndromes: A Multicenter Study of the Lysosomal Disease Network
NCT01586871
University of Minnesota
TerminatedStudy to Detect Unrecognized Mucopolysaccharidosis in Children Visiting Rheumatology, Hand or Skeletal Dysplas
NCT01675674
National MPS Society
CompletedLongitudinal Study of Bone Disease in Children with Mucopolysaccharidoses (MPS) I, II, and VI
NCT01521429
Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center