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Trials / Conditions / Molybdenum Cofactor Deficiency, Type A

Molybdenum Cofactor Deficiency, Type A

4 registered clinical trials studyying Molybdenum Cofactor Deficiency, Type A1 currently recruiting.

StatusTrialSponsorPhase
Enrolling By InvitationEarly Check: Expanded Screening in Newborns
NCT03655223
RTI International
CompletedStudy of ORGN001 (Formerly ALXN1101) in Neonates, Infants and Children With Molybdenum Cofactor Deficiency (MO
NCT02629393
Origin BiosciencesPhase 2 / Phase 3
CompletedSafety & Efficacy Study of ORGN001 (Formerly ALXN1101) in Pediatric Patients With MoCD Type A Currently Treate
NCT02047461
Origin BiosciencesPhase 2
WithdrawnStudy of cPMP (Precusor Z) to Treat Molybdenum Cofactor Deficiency (MoCD) Type A
NCT00957749
Orphatech Pharmaceuticals, GmbHPhase 1 / Phase 2