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Trials / Conditions / Hoyeraal Hreidarsson Syndrome

Hoyeraal Hreidarsson Syndrome

3 registered clinical trials studyying Hoyeraal Hreidarsson Syndrome2 currently recruiting.

StatusTrialSponsorPhase
RecruitingNucleoside Therapy in Patients With Telomere Biology Disorders
NCT06817590
Suneet AgarwalPhase 1
RecruitingRegenerative Medicine to Restore Hematopoiesis and Immune Function in Immunodeficiencies and Inherited Bone Ma
NCT04232085
Sidney Kimmel Comprehensive Cancer Center at Johns HopkinsPhase 2
Active Not RecruitingRadiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita
NCT01659606
Boston Children's HospitalPhase 2