Trials / Conditions / Hereditary Amyloidosis, Transthyretin-Related
Hereditary Amyloidosis, Transthyretin-Related
4 registered clinical trials studyying Hereditary Amyloidosis, Transthyretin-Related — 2 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Active Not Recruiting | Validation of a Questionnaire for Quality of Life Assessment in Patients With Transthyretin Amyloidosis. NCT07080268 | Hospital General de Niños Pedro de Elizalde | — |
| Recruiting | Phenotypic Manifestations of Hereditary ATTR Amyloidosis NCT07124377 | Hospital 9 de Julio de Las Breñas | — |
| Recruiting | Observational Study of Neurofilament Light Chain (NfL) as a Biomarker in Asymptomatic Carriers of the Transthy NCT06360289 | Alnylam Pharmaceuticals | — |
| Completed | Early Detection of Neuropathy in ATTRv NCT05311488 | University of Pennsylvania | — |