Trials / Conditions / GM1 Gangliosidoses
GM1 Gangliosidoses
3 registered clinical trials studyying GM1 Gangliosidoses — 2 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Not Yet Recruiting | Prenatal Intravenous Gene Transfer With an AAV9 Vector Expressing Human Beta-galactosidase in Type I and Type NCT07479953 | Tippi Mackenzie | Phase 1 |
| Terminated | Synergistic Enteral Regimen for Treatment of the Gangliosidoses NCT02030015 | University of Minnesota | Phase 4 |
| Recruiting | Longitudinal Study of Neurodegenerative Disorders NCT03333200 | University of Pittsburgh | — |