Trials / Sponsors / Tippi Mackenzie
Tippi Mackenzie
Academic / Other · 1 registered clinical trial — 1 currently recruiting.
| Status | Trial | Phase | Started |
|---|---|---|---|
| Not Yet Recruiting | Prenatal Intravenous Gene Transfer With an AAV9 Vector Expressing Human Beta-galactosidase in Type I and Type GM1 Gangliosidoses, GM1 Gangliosidosis, Type I, GM1 Gangliosidosis, Type 2 | Phase 1 | 2026-06-01 |