Trials / Conditions / Genetic Disease, Inborn

Genetic Disease, Inborn

4 registered clinical trials studyying Genetic Disease, Inborn — 2 currently recruiting.

Status	Trial	Sponsor	Phase
Recruiting	A Phase 3 Study of NTLA-2001 in ATTRv-PN NCT06672237	Intellia Therapeutics	Phase 3
Completed	Evaluate the Effect of Obicetrapib in Patients With HeFH on Top of Maximum Tolerated Lipid-Modifying Therapies NCT05425745	NewAmsterdam Pharma	Phase 3
Completed	A Study Comparing the Quality of Life of Patients in the Treatment of Eczema by Pediatric Generalists and Spec NCT02916888	Yale University	—
Recruiting	Recruitment and Apheresis Collection of Peripheral Blood Hematopoietic Stem Cells, Mononuclear Cells and Granu NCT00001405	National Institute of Allergy and Infectious Diseases (NIAID)	—