Trials / Conditions / Gaucher Disease, Type 2
Gaucher Disease, Type 2
3 registered clinical trials studyying Gaucher Disease, Type 2 — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Recruiting | PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders) NCT04532047 | University of California, San Francisco | Phase 1 |
| Active Not Recruiting | Phase 1/2 Clinical Trial of PR001 in Infants With Type 2 Gaucher Disease (PROVIDE) NCT04411654 | Prevail Therapeutics | Phase 1 / Phase 2 |
| Completed | Natural History Study for Pediatric Patients With Early Onset of Either GM1 Gangliosidosis, GM2 Gangliosidoses NCT04470713 | Idorsia Pharmaceuticals Ltd. | — |