Clinical Trials Directory

Trials / Conditions / Gangliosidoses, GM2

Gangliosidoses, GM2

3 registered clinical trials studyying Gangliosidoses, GM21 currently recruiting.

StatusTrialSponsorPhase
RecruitingA Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile For
NCT07082543
Azafaros A.G.Phase 3
CompletedPyrimethamine as a Treatment for Late-Onset GM2-gangliosidosis (Tay-Sachs and Sandhoff Disease)
NCT01102686
The Hospital for Sick ChildrenPhase 1 / Phase 2
CompletedPharmacokinetics and Tolerability of Zavesca® (Miglustat) In Patients With Juvenile GM2 Gangliosidosis
NCT00418847
The Hospital for Sick ChildrenPhase 2