Trials / Conditions / Dysferlinopathy
Dysferlinopathy
6 registered clinical trials studyying Dysferlinopathy — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Completed | Observational Cohort Study of Dysferlinopathy in China NCT07035145 | Peking University First Hospital | — |
| Enrolling By Invitation | Clinical, Immunological, Morphological and Genetic Characteristics of Patients With Dysferlinopathy (LGMD R2) NCT04824040 | Artgen Biotech | — |
| Completed | rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies NCT02710500 | Sarepta Therapeutics, Inc. | Phase 1 |
| Terminated | Proteasomal Inhibition for Patients With Mis-sense Mutated Dysferlin NCT01863004 | University Hospital, Basel, Switzerland | Phase 1 |
| Unknown | Clinical Outcome Study for Dysferlinopathy NCT01676077 | Newcastle-upon-Tyne Hospitals NHS Trust | — |
| Completed | Deflazacort in Dysferlinopathies NCT00527228 | Ludwig-Maximilians - University of Munich | Phase 2 / Phase 3 |