Clinical Trials Directory

Trials / Conditions / Barth Syndrome

Barth Syndrome

9 registered clinical trials studyying Barth Syndrome — 3 currently recruiting.

StatusTrialSponsorPhase
Not Yet RecruitingPh3b/4 Trial in Patients With Barth Syndrome
NCT07531251
Stealth BioTherapeutics Inc.Phase 4
Enrolling By InvitationEarly Check: Expanded Screening in Newborns
NCT03655223
RTI International—
CompletedA Trial to Evaluate Safety, Tolerability and Efficacy of Elamipretide in Subjects With Barth Syndrome
NCT03098797
Stealth BioTherapeutics Inc.Phase 2 / Phase 3
CompletedResistance Exercise in Barth Syndrome
NCT01629459
Washington University School of MedicineN/A
CompletedHeart and Muscle Metabolism in Barth Syndrome
NCT01625663
Duke University—
CompletedExercise Training in Barth Syndrome
NCT01194141
Washington University School of MedicineN/A
RecruitingGlobal Registry and Natural History Study for Mitochondrial Disorders
NCT05554835
LMU Klinikum—
AvailableAn Intermediate Size Expanded Access Protocol of Elamipretide
NCT04689360
Stealth BioTherapeutics Inc.—
No Longer AvailableCompassionate Use of Triheptanoin (C7) for Inherited Disorders of Energy Metabolism
NCT01461304
Jerry Vockley, MD, PhD—