Trials / Conditions / Aspartylglucosaminuria
Aspartylglucosaminuria
6 registered clinical trials studyying Aspartylglucosaminuria — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Not Yet Recruiting | Safety and Efficacy of scAAV9/AGA Gene Therapy in Participants With Aspartylglucosaminuria (AGU) NCT07530796 | Rare Trait Hope | Phase 1 / Phase 2 |
| Terminated | A Natural History Study of Aspartylglucosaminuria NCT03853876 | Neurogene Inc. | — |
| Active Not Recruiting | MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis NCT02171104 | Masonic Cancer Center, University of Minnesota | Phase 2 |
| Completed | Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders NCT01043640 | Masonic Cancer Center, University of Minnesota | Phase 2 |
| Completed | Longitudinal Studies of the Glycoproteinoses NCT01891422 | Greenwood Genetic Center | — |
| Terminated | Hematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism NCT00668564 | Masonic Cancer Center, University of Minnesota | Phase 2 |