Clinical Trials Directory

Trials / Sponsors / Neurogene Inc.

Neurogene Inc.

Industry · 6 registered clinical trials1 currently recruiting.

StatusTrialPhaseStarted
RecruitingA Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome
Rett Syndrome
Phase 32023-06-13
Active Not RecruitingGene Therapy Study for Children With CLN5 Batten Disease
Neuronal Ceroid Lipofuscinosis CLN5
Phase 1 / Phase 22022-01-31
CompletedNL-201 Monotherapy and in Combination With Pembrolizumab in Patients With Relapsed or Refractory Cancer
Solid Tumor, Advanced Solid Tumor
Phase 12021-04-26
TerminatedA Natural History Study of Charcot-Marie-Tooth 4J (CMT4J)
Charcot-Marie-Tooth Disease, Hereditary Motor and Sensory Neuropathy IV
2019-07-18
TerminatedA Natural History Study of Aspartylglucosaminuria
Aspartylglucosaminuria, Aspartylglucosamidase (AGA) Deficiency, Lysosomal Storage Diseases
2019-04-18
CompletedA Natural History Study of Neuronal Ceroid Lipofuscinosis Type 5 (CLN5)
Ceroid Lipofuscinosis, Neuronal 5
2019-03-13