Clinical Trials Directory

Trials / Conditions / ADA-SCID

ADA-SCID

6 registered clinical trials studyying ADA-SCID1 currently recruiting.

StatusTrialSponsorPhase
CompletedEZN-2279 in Patients With ADA-SCID
NCT01420627
Leadiant Biosciences, Inc.Phase 3
CompletedTreatment of SCID Due to ADA Deficiency With Autologous Transplantation of Cord Blood or Hematopoietic CD 34+
NCT02022696
National Human Genome Research Institute (NHGRI)Phase 1
CompletedAutologous CD34+ Hematopoietic Stem Cells Transduced ex Vivo With Elongation Factor 1 Alpha Shortened (EFS) Le
NCT01852071
University of California, Los AngelesPhase 1 / Phase 2
UnknownPatients Treated for SCID (1968-Present)
NCT01346150
National Institute of Allergy and Infectious Diseases (NIAID)
Enrolling By InvitationNatural History Study of SCID Disorders
NCT01186913
National Institute of Allergy and Infectious Diseases (NIAID)
WithdrawnQuality of Life and Neuropsychiatric Sequelae in Patients Treated With Gene Therapy for ADA-SCID and in Their
NCT01182857
National Human Genome Research Institute (NHGRI)