Trials / Conditions / Acid Maltase Deficiency
Acid Maltase Deficiency
5 registered clinical trials studyying Acid Maltase Deficiency — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Not Yet Recruiting | Treatment Frequency Reduction in Pompe Disease NCT06575829 | Erasmus Medical Center | Phase 4 |
| Active Not Recruiting | A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE) NCT04093349 | Spark Therapeutics, Inc. | Phase 1 / Phase 2 |
| Completed | Neutralizing Antibody Seroprevalence Study With a Retrospective Component in Participants With Late-Onset Pomp NCT03893240 | Spark Therapeutics, Inc. | N/A |
| Completed | Safety and Efficacy Evaluation of Repeat neoGAA Dosing in Late Onset Pompe Disease Patients. NCT01898364 | Genzyme, a Sanofi Company | Phase 1 |
| Terminated | A Noninferiority Study of Alglucosidase Alfa Manufactured at the 160 L and 4000 L Scales in Treatment Naïve Pa NCT01597596 | Genzyme, a Sanofi Company | Phase 4 |