Trials / Completed
CompletedNCT07474311
A Real-World Study of Clinical Use of Available Treatments for Pediatric Patients With Spinal Muscular Atrophy
Real-World Evidence of Clinical Use of Available Treatments for Pediatric Patients With Spinal Muscular Atrophy (SMA): A Multi-Site Retrospective Analysis Based on REaDY Registry
- Status
- Completed
- Phase
- —
- Study type
- Observational
- Enrollment
- 213 (actual)
- Sponsor
- Novartis Pharmaceuticals · Industry
- Sex
- All
- Age
- 18 Years
- Healthy volunteers
- Not accepted
Summary
The aim of this study was to evaluate real-world treatment patterns and clinical outcomes in pediatric SMA patients in the Czech and Slovak Republics, using data from the Registry of muscular Dystrophy (REaDY).
Conditions
Timeline
- Start date
- 2011-11-22
- Primary completion
- 2025-03-13
- Completion
- 2025-03-13
- First posted
- 2026-03-16
- Last updated
- 2026-03-20
Locations
1 site across 1 country: Czechia
Source: ClinicalTrials.gov record NCT07474311. Inclusion in this directory is not an endorsement.