Trials / Not Yet Recruiting
Not Yet RecruitingNCT07396285
UCSF Center for Genome Surgery Biobank and Registry
- Status
- Not Yet Recruiting
- Phase
- —
- Study type
- Observational
- Enrollment
- 10,000 (estimated)
- Sponsor
- University of California, San Francisco · Academic / Other
- Sex
- All
- Age
- —
- Healthy volunteers
- Accepted
Summary
Gene editing approaches (including but not limited to: CRISPR, LNP, AAV, RNAi etc.) for the medical specialty of interventional genomics require (1) determination of the clinical relevance of genomic variants and (2) systematic evaluation of the 'editability' of those variants. Here, we seek to use in silico and in vitro analyses of genomic, cellular, and clinical data/specimens to (1) identify novel pathogenic variants underlying diseases and (2) examine the specificity and efficacy of various gene editing components across the entire human genomic landscape.
Conditions
Timeline
- Start date
- 2026-05-01
- Primary completion
- 2050-12-01
- Completion
- 2050-12-01
- First posted
- 2026-02-09
- Last updated
- 2026-02-09
Locations
1 site across 1 country: United States
Source: ClinicalTrials.gov record NCT07396285. Inclusion in this directory is not an endorsement.