Trials / No Longer Available
No Longer AvailableNCT07159139
Vatiquinone Expanded Access Protocol
Expanded Access Protocol for Vatiquinone in Previously Treated Patients With Inherited Mitochondrial Disease
- Status
- No Longer Available
- Phase
- —
- Study type
- Expanded Access
- Enrollment
- —
- Sponsor
- Medical University of South Carolina · Academic / Other
- Sex
- All
- Age
- 1 Year
- Healthy volunteers
- —
Summary
The purpose of this study is to provide participants who successfully completed the study titled "An Open-label, Safety Study for Previously Treated Vatiquinone (PTC743) Subjects With Inherited Mitochondrial Disease" with liquid Vatiquinone through an intermediate patient population expanded access protocol.
Detailed description
This expanded access protocol serves to make Vatiquinone accessible to subjects with inherited mitochondrial disease who previously participated in a Vatiquinone clinical trial at the Medical University of South Carolina (MUSC) who in the opinion of the investigator would benefit from continued access to liquid Vatiquinone.
Conditions
Interventions
| Type | Name | Description |
|---|---|---|
| DRUG | Vatiquinone | Vatiquinone will be administered per dose and schedule specified in the arm description. |
Timeline
- First posted
- 2025-09-08
- Last updated
- 2026-04-09
Source: ClinicalTrials.gov record NCT07159139. Inclusion in this directory is not an endorsement.