Trials / Not Yet Recruiting
Not Yet RecruitingNCT06774703
Nemaline Myopathy Clinical Research Network (NM-CTRN)
- Status
- Not Yet Recruiting
- Phase
- —
- Study type
- Observational
- Enrollment
- 50 (estimated)
- Sponsor
- Stanford University · Academic / Other
- Sex
- All
- Age
- 0 Years – 18 Years
- Healthy volunteers
- Not accepted
Summary
The goal of this study is to establish a research network to help define the natural disease history and clinical outcome measures for Nemaline Myopathy (NM).
Detailed description
The long-term aim of this study is to incorporate these outcome measures into clinical trials for NM therapies. Outcome measures to be assessed will be dependent on the participant's age and functional status. Follow-up visits will be conducted either every 3 or 6 months, dependent on age, for a total of 3 years.
Conditions
Timeline
- Start date
- 2025-01-01
- Primary completion
- 2029-12-01
- Completion
- 2029-12-01
- First posted
- 2025-01-14
- Last updated
- 2025-01-14
Locations
6 sites across 2 countries: United States, Canada
Source: ClinicalTrials.gov record NCT06774703. Inclusion in this directory is not an endorsement.