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Trials / Enrolling By Invitation

Enrolling By InvitationNCT06679946

A Study to Evaluate Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy

An Open-Label Extension Study to Assess the Safety and Efficacy of Vutrisiran in Patients With Transthyretin Amyloidosis With Cardiomyopathy (ATTR Amyloidosis With Cardiomyopathy)

Status
Enrolling By Invitation
Phase
Phase 3
Study type
Interventional
Enrollment
700 (estimated)
Sponsor
Alnylam Pharmaceuticals · Industry
Sex
All
Age
18 Years
Healthy volunteers
Not accepted

Summary

The purpose of this study is to obtain safety, efficacy, and pharmacodynamic data on the use of vutrisiran in patients with ATTR amyloidosis with cardiomyopathy who continued on extended use of vutrisiran, or switched from patisiran.

Conditions

Interventions

TypeNameDescription
DRUGVutrisiranVutrisiran administered SC q3M

Timeline

Start date
2024-12-03
Primary completion
2028-03-31
Completion
2028-03-31
First posted
2024-11-08
Last updated
2026-02-20

Locations

87 sites across 17 countries: United States, Argentina, Austria, Belgium, Brazil, Czechia, Denmark, France, Italy, Netherlands, Norway, Portugal, South Korea, Spain, Sweden, Taiwan, United Kingdom

Regulatory

Source: ClinicalTrials.gov record NCT06679946. Inclusion in this directory is not an endorsement.