Trials / Recruiting
RecruitingNCT06591806
An Observational Study in Children and Adults With Stargardt Disease
A Multicenter, Prospective, Longitudinal, Observational Study in Children and Adults With Stargardt Disease Related Atrophy Secondary to Biallelic Mutations in the ABCA4 Gene
- Status
- Recruiting
- Phase
- —
- Study type
- Observational
- Enrollment
- 80 (estimated)
- Sponsor
- AAVantgarde Bio Srl · Industry
- Sex
- All
- Age
- 8 Years – 50 Years
- Healthy volunteers
- Not accepted
Summary
This multicenter, prospective, longitudinal, observational study in approximately 80 subjects with Stargardt disease secondary to biallelic mutations in the ABCA4 gene (STGD1) aims to evaluate prognostic factors of disease progression, and to further characterize the patient population for future clinical studies.
Conditions
Timeline
- Start date
- 2024-05-01
- Primary completion
- 2027-06-30
- Completion
- 2027-06-30
- First posted
- 2024-09-19
- Last updated
- 2025-08-28
Locations
2 sites across 2 countries: United States, Norway
Source: ClinicalTrials.gov record NCT06591806. Inclusion in this directory is not an endorsement.