Trials / Active Not Recruiting
Active Not RecruitingNCT06095388
Phase I/II Study of JR-441 in Patients With Mucopolysaccharidosis Type IIIA
Phase I/II Study of Weekly Infusions of JR-441 in Patients With Mucopolysaccharidosis Type IIIA
- Status
- Active Not Recruiting
- Phase
- Phase 1 / Phase 2
- Study type
- Interventional
- Enrollment
- 15 (actual)
- Sponsor
- JCR Pharmaceuticals Co., Ltd. · Industry
- Sex
- All
- Age
- 1 Year – 18 Years
- Healthy volunteers
- Not accepted
Summary
A Phase I/ II, open-label, randomized, 2-arm study, designed to evaluate the safety and explore efficacy of the study drug in development for the treatment of MPS IIIA patients.
Conditions
Interventions
| Type | Name | Description |
|---|---|---|
| DRUG | JR-441 | IV infusion |
| DRUG | JR-441 | IV infusion |
| DRUG | JR-441 | IV infusion |
Timeline
- Start date
- 2023-10-04
- Primary completion
- 2029-10-31
- Completion
- 2029-10-31
- First posted
- 2023-10-23
- Last updated
- 2025-08-26
Locations
1 site across 1 country: Germany
Source: ClinicalTrials.gov record NCT06095388. Inclusion in this directory is not an endorsement.