Clinical Trials Directory

Trials / No Longer Available

No Longer AvailableNCT06028594

Compassionate Use of Pozelimab and Cemdisiran Combination Therapy in Patients With Paroxysmal Nocturnal Hemoglobinuria

An Expanded Access Program of Pozelimab and Cemdisiran Combination Therapy in Patients With Paroxysmal Nocturnal Hemoglobinuria

Status
No Longer Available
Phase
Study type
Expanded Access
Enrollment
Sponsor
Regeneron Pharmaceuticals · Industry
Sex
All
Age
18 Years
Healthy volunteers

Summary

This program is designed to provide access to pozelimab and cemdisiran and document the long-term safety of pozelimab and cemdisiran combination therapy in patients with paroxysmal nocturnal hemoglobinuria (PNH). PNH is a rare immune disease that causes red blood cells in your body to break apart.

Conditions

Interventions

TypeNameDescription
DRUGPozelimabSubcutaneous (SC) administration
DRUGCemdisiranSubcutaneous (SC) administration

Timeline

First posted
2023-09-08
Last updated
2025-10-20

Source: ClinicalTrials.gov record NCT06028594. Inclusion in this directory is not an endorsement.