Trials / Unknown
UnknownNCT05705674
The Natural History Study of Patients With Sanfilippo Disease(s) (MPS3)
- Status
- Unknown
- Phase
- —
- Study type
- Observational
- Enrollment
- 6 (estimated)
- Sponsor
- Lysosomal and Rare Disorders Research and Treatment Center, Inc. · Academic / Other
- Sex
- All
- Age
- 5 Years – 99 Years
- Healthy volunteers
- Not accepted
Summary
The natural history study of patients with Sanfilippo disease(s) (MPS3)
Detailed description
This is a natural history study of patients with Sanfilippo Disease (MPS3). Patients will be followed over the course of 6 months in which they have blood and urine collected, hearing assessment, complete questionnaires and are evaluated by the Principal Investigator.
Conditions
Timeline
- Start date
- 2023-05-01
- Primary completion
- 2024-12-01
- Completion
- 2024-12-01
- First posted
- 2023-01-31
- Last updated
- 2024-03-12
Locations
1 site across 1 country: United States
Source: ClinicalTrials.gov record NCT05705674. Inclusion in this directory is not an endorsement.