NCT05695560

A Survey to Describe the Experience and Unmet Needs of Persons Living With Von Willebrand Disease (VWD) and Their Caregivers

Unmet Needs of Patients Living With Von Willebrand Disease and Their Caregivers: Qualitative Survey on Current Standard of Care in Canada

• Status: Completed
• Phase: —
• Study type: Observational
• Enrollment: 12 (actual)
• Sponsor: Takeda · Industry
• Sex: All
• Age: 0 Years – 50 Years
• Healthy volunteers: Not accepted

Summary

The main aim of this study is to describe the experience and unmet needs of persons living with VWD and their caregivers in Canada. The survey is planned to be done in two phases: The first phase will be directed at adult participants; the second phase will focus on children and teenagers. At the end of the first phase the Sponsor will decide if the second phase will be started. Participants and their caregivers will be asked to answer a set of questions either using an online questionnaire or through interviews. The participant/caregiver's perception, experience, satisfaction, and unmet needs, and need for new treatments or new indications will be determined based on their responses to the questions.

Detailed description

This study is a non-interventional, prospective, qualitative survey to know the unmet needs of participants living with VWD and their caregivers. The study will enroll approximately 49 patients, taking into scope both the participant's and caregiver's perspectives, and is planned to be conducted in two phases: Phase 1: Adult Participants Phase 2: Pediatric Participants The decision to proceed with Phase 2 will be determined at the completion of Phase 1. This multi-center trial will be conducted in Canada. The overall time for data collection in this study is approximately 9 months.

Conditions

• Von Willebrand Disease (VWD)

Interventions

Type	Name	Description
OTHER	No Intervention	As this is an observational study, no intervention will be administered.

Timeline

• Start date: 2023-02-24
• Primary completion: 2023-11-30
• Completion: 2023-11-30
• First posted: 2023-01-25
• Last updated: 2023-12-20

Locations

1 site across 1 country: Canada