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Active Not RecruitingNCT05567458

A Study to Evaluate Luspatercept (ACE-536) in Chinese Participants Who Require Regular Red Blood Cell Transfusions Due to Beta (β)-Thalassemia.

A Phase 2, Double-blind, Randomized, Placebo-controlled, Multicenter Study to Evaluate the Efficacy, Safety and Pharmacokinetics of Luspatercept (ACE-536) in Chinese Adult Subjects Who Require Regular Red Blood Cell Transfusions Due to Beta (β)-Thalassemia

Status
Active Not Recruiting
Phase
Phase 2
Study type
Interventional
Enrollment
94 (actual)
Sponsor
Bristol-Myers Squibb · Industry
Sex
All
Age
18 Years
Healthy volunteers
Not accepted

Summary

The purpose of this study is to evaluate the efficacy, safety and pharmacokinetics of luspatercept plus best supportive care (BSC) versus placebo plus BSC in participants who require regular red blood cell transfusions due to β-thalassemia.

Conditions

Interventions

TypeNameDescription
DRUGLuspaterceptSpecified dose on specified days
DRUGPlaceboSpecified dose on specified days

Timeline

Start date
2022-10-17
Primary completion
2025-08-01
Completion
2026-08-01
First posted
2022-10-05
Last updated
2025-08-12

Locations

10 sites across 1 country: China

Regulatory

Source: ClinicalTrials.gov record NCT05567458. Inclusion in this directory is not an endorsement.

A Study to Evaluate Luspatercept (ACE-536) in Chinese Participants Who Require Regular Red Blood Cell Transfusions Due t (NCT05567458) · Clinical Trials Directory