Trials / Active Not Recruiting
Active Not RecruitingNCT05506254
Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy
A Long-term Follow-up Study of Patients in LogicBio Clinical Trials for Methylmalonic Acidemia Characterized by MMUT Mutations Who Received hLB-001
- Status
- Active Not Recruiting
- Phase
- —
- Study type
- Observational
- Enrollment
- 4 (actual)
- Sponsor
- Alexion Pharmaceuticals, Inc. · Industry
- Sex
- All
- Age
- 18 Years
- Healthy volunteers
- Not accepted
Summary
This is a non-interventional long-term follow-up study of patients who have participated in LogicBio studies for the treatment of MMA and received hLB-001
Detailed description
Patients will be followed for a period of 15 years which includes the duration of time that the patient was in the treatment study.
Conditions
Interventions
| Type | Name | Description |
|---|---|---|
| DRUG | hLB-001 | hLB-001 gene therapy |
Timeline
- Start date
- 2022-07-15
- Primary completion
- 2037-01-01
- Completion
- 2037-01-01
- First posted
- 2022-08-18
- Last updated
- 2026-02-05
Locations
4 sites across 1 country: United States
Regulatory
- FDA-regulated drug study
Source: ClinicalTrials.gov record NCT05506254. Inclusion in this directory is not an endorsement.