Clinical Trials Directory

Trials / Recruiting

RecruitingNCT05312879

Phase 2/3 Adaptive Study of VX-147 in Adult and Pediatric Participants With APOL1-Mediated Proteinuric Kidney Disease

A Phase 2/3 Adaptive, Double-blind, Placebo-Controlled Study to Evaluate the Efficacy and Safety of VX-147 in Adult and Pediatric Subjects With APOL1-mediated Proteinuric Kidney Disease

Status
Recruiting
Phase
Phase 2 / Phase 3
Study type
Interventional
Enrollment
466 (estimated)
Sponsor
Vertex Pharmaceuticals Incorporated · Industry
Sex
All
Age
10 Years – 65 Years
Healthy volunteers
Not accepted

Summary

The purpose of this study is to evaluate the efficacy, safety, tolerability, and pharmacokinetics (PK) of VX-147 in adult and pediatric participants with apolipoprotein L1 (APOL1)-mediated proteinuric kidney disease.

Conditions

Interventions

TypeNameDescription
DRUGVX-147Tablets for oral administration.
DRUGPlaceboTablets for oral administration.

Timeline

Start date
2022-03-30
Primary completion
2028-06-02
Completion
2030-05-07
First posted
2022-04-06
Last updated
2026-04-17

Locations

318 sites across 13 countries: United States, Belgium, Brazil, Canada, Colombia, France, Ghana, Netherlands, Nigeria, Portugal, Puerto Rico, Spain, United Kingdom

Regulatory

Source: ClinicalTrials.gov record NCT05312879. Inclusion in this directory is not an endorsement.