Trials / Enrolling By Invitation
Enrolling By InvitationNCT05236595
Research for Individualized Therapeutics in Rare Genetic Disease
- Status
- Enrolling By Invitation
- Phase
- —
- Study type
- Observational
- Enrollment
- 50 (estimated)
- Sponsor
- Mayo Clinic · Academic / Other
- Sex
- All
- Age
- —
- Healthy volunteers
- Accepted
Summary
The purpose of this research study is to identify individuals that have a rare genetic disease without an adequate therapeutic strategy that might be treatable with drug developed to target the disease-causing genetic alteration.
Conditions
Interventions
| Type | Name | Description |
|---|---|---|
| OTHER | Individualized drug matching per genetic disease | Patient phenotype and samples will be evaluated for individualized therapeutic drug development |
Timeline
- Start date
- 2021-11-24
- Primary completion
- 2026-11-01
- Completion
- 2026-11-01
- First posted
- 2022-02-11
- Last updated
- 2026-01-20
Locations
3 sites across 1 country: United States
Source: ClinicalTrials.gov record NCT05236595. Inclusion in this directory is not an endorsement.