Clinical Trials Directory

Trials / Recruiting

RecruitingNCT05005975

Extension Study to Evaluate Safety and Tolerability of Oral Dersimelagon (MT-7117) in Subjects With Erythropoietic Protoporphyria (EPP) or X-Linked Protoporphyria (XLP)

A Phase 3, Multicenter, Open-label, Long-term, Extension Study to Evaluate Safety and Tolerability of Oral Dersimelagon (MT-7117) in Subjects With Erythropoietic Protoporphyria (EPP) or X-Linked Protoporphyria (XLP)

Status
Recruiting
Phase
Phase 3
Study type
Interventional
Enrollment
301 (estimated)
Sponsor
Tanabe Pharma America, Inc. · Industry
Sex
All
Age
12 Years – 75 Years
Healthy volunteers
Not accepted

Summary

To evaluate the long-term safety and tolerability of oral dersimelagon.

Conditions

Interventions

TypeNameDescription
DRUGMT-7117MT-7117

Timeline

Start date
2021-08-10
Primary completion
2027-12-01
Completion
2027-12-01
First posted
2021-08-16
Last updated
2025-12-11

Locations

51 sites across 15 countries: United States, Australia, Belgium, Canada, Czechia, France, Germany, Italy, Japan, Netherlands, Norway, Poland, Spain, Sweden, United Kingdom

Regulatory

Source: ClinicalTrials.gov record NCT05005975. Inclusion in this directory is not an endorsement.