Trials / Withdrawn
WithdrawnNCT04977648
Natural History Study of Patients With Centronuclear Myopathies
A Prospective, Longitudinal Study of the Natural History and Functional Status of Patients With Centronuclear Myopathies
- Status
- Withdrawn
- Phase
- —
- Study type
- Observational
- Enrollment
- 0 (actual)
- Sponsor
- Dynacure · Industry
- Sex
- All
- Age
- 0 Months
- Healthy volunteers
- Not accepted
Summary
This is a prospective, longitudinal study of the natural disease course intended to recruit approximately 60 patients with centronuclear myopathies (CNM) in Europe and the United States. The duration of the study, including the enrollment period, will be approximately 4 years. Data from the study will be used to characterize the natural disease course of CNM, to identify prognostic variables of the disease and to determine the best outcome measure(s) for the evaluation of future therapeutic approaches.
Conditions
Timeline
- Start date
- 2022-09-01
- Primary completion
- 2026-03-01
- Completion
- 2026-03-01
- First posted
- 2021-07-27
- Last updated
- 2022-07-11
Source: ClinicalTrials.gov record NCT04977648. Inclusion in this directory is not an endorsement.