Clinical Trials Directory

Trials / Completed

CompletedNCT04808297

Trehalose in Subjects With Neuronal Ceroid Lipofuscinoses

A Study in Subjects With Neuronal Ceroid Lipofuscinoses Taking Trehalose

Status
Completed
Phase
Study type
Observational
Enrollment
8 (actual)
Sponsor
IRCCS Fondazione Stella Maris · Academic / Other
Sex
All
Age
7 Years – 45 Years
Healthy volunteers
Not accepted

Summary

Neuronal Ceroid Lipofuscinoses (NCL) or Batten's disease are the most common juvenile neurodegenerative disease, characterized by early blindness, movement disorders, cognitive and behavioral impairment, epilepsy, and retinopathy. This study aims to collect clinical and laboratory data of patients with NCL taking Trehalose.

Detailed description

This study aims to collect clinical and laboratory data of patients with NCL taking Trehalose.

Conditions

Timeline

Start date
2020-08-01
Primary completion
2021-07-01
Completion
2021-10-01
First posted
2021-03-22
Last updated
2022-04-11

Locations

1 site across 1 country: Italy

Source: ClinicalTrials.gov record NCT04808297. Inclusion in this directory is not an endorsement.