Clinical Trials Directory

Trials / Completed

CompletedNCT04458051

Primary Progressive Multiple Sclerosis (PPMS) Study of Bruton's Tyrosine Kinase (BTK) Inhibitor Tolebrutinib (SAR442168) (PERSEUS)

A Phase 3, Randomized, Double-blind, Efficacy and Safety Study Comparing SAR442168 to Placebo in Participants With Primary Progressive Multiple Sclerosis (PERSEUS)

Status
Completed
Phase
Phase 3
Study type
Interventional
Enrollment
767 (actual)
Sponsor
Sanofi · Industry
Sex
All
Age
18 Years – 55 Years
Healthy volunteers
Not accepted

Summary

Primary Objective: To determine the efficacy of SAR442168 compared to placebo in delaying disability progression in primary progressive multiple sclerosis (PPMS) Secondary Objectives: To evaluate efficacy of SAR442168 compared to placebo on clinical endpoints, magnetic resonance imaging (MRI) lesions, cognitive performance, physical function, and quality of life To evaluate safety and tolerability of SAR442168 To evaluate population pharmacokinetics (PK) of SAR442168 in PPMS and its relationship to efficacy and safety To evaluate pharmacodynamics of SAR442168

Detailed description

Study duration will vary per participant in this event driven trial with a treatment duration of approximately 12 to 60 months.

Conditions

Interventions

TypeNameDescription
DRUGTolebrutinibPharmaceutical form: Film-coated Tablet Route of administration: Oral
DRUGPlaceboPharmaceutical form: Film-coated Tablet Route of administration: Oral

Timeline

Start date
2020-08-13
Primary completion
2025-11-14
Completion
2025-11-14
First posted
2020-07-07
Last updated
2026-01-07

Locations

277 sites across 42 countries: United States, Argentina, Australia, Austria, Belarus, Belgium, Brazil, Bulgaria, Canada, Chile, China, Colombia, Croatia, Czechia, Denmark, Estonia, France, Georgia, Germany, Greece, Hungary, India, Israel, Italy, Japan, Latvia, Mexico, Netherlands, Norway, Peru, Poland, Portugal, Romania, Russia, Serbia, South Africa, Spain, Sweden, Thailand, Turkey (Türkiye), Ukraine, United Kingdom

Regulatory

Source: ClinicalTrials.gov record NCT04458051. Inclusion in this directory is not an endorsement.