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CompletedNCT04035811

Prospective Clinical Assessment Study in Children With Achondroplasia (ACH)

Prospective Clinical Assessment Study in Children With Achondroplasia: The PROPEL Trial

Status
Completed
Phase
Study type
Observational
Enrollment
271 (actual)
Sponsor
QED Therapeutics, a BridgeBio company · Industry
Sex
All
Age
30 Months – 17 Years
Healthy volunteers
Not accepted

Summary

This is a long-term, multi-center, observational study in children 2.5 to \<17 years with achondroplasia (ACH). The objective is to evaluate growth, ACH-related medical complications, assessments of health-related quality of life, body pain, functional abilities, cognitive functions, and treatments of study participants. No study medication will be administered.

Conditions

Timeline

Start date
2019-08-12
Primary completion
2025-08-27
Completion
2025-08-27
First posted
2019-07-29
Last updated
2026-04-03

Locations

32 sites across 11 countries: United States, Argentina, Australia, Canada, France, Germany, Italy, Norway, Singapore, Spain, United Kingdom

Source: ClinicalTrials.gov record NCT04035811. Inclusion in this directory is not an endorsement.