Trials / Recruiting
RecruitingNCT04012671
A Registered Cohort Study on Duchenne Muscular Dystrophy
- Status
- Recruiting
- Phase
- —
- Study type
- Observational
- Enrollment
- 2,000 (estimated)
- Sponsor
- Ning Wang, MD., PhD. · Academic / Other
- Sex
- All
- Age
- 2 Years
- Healthy volunteers
- Not accepted
Summary
Dystrophinopathy is a term of X-linked recessive genetic disease, including Duchenne Muscular Dystrophy, Becker Muscular Dystrophy, and the X-linked dilated cardiomyopathy. The aim of this study is to determine the clinical spectrum and natural progression of dystrophinopathy in a prospective multicenter natural history study, to assess the clinical, genetic of patients with dystrophinopathy to optimize clinical management.
Conditions
Timeline
- Start date
- 2019-07-01
- Primary completion
- 2039-12-31
- Completion
- 2049-12-31
- First posted
- 2019-07-09
- Last updated
- 2021-03-22
Locations
1 site across 1 country: China
Source: ClinicalTrials.gov record NCT04012671. Inclusion in this directory is not an endorsement.