Clinical Trials Directory

Trials / Completed

CompletedNCT03783377

Study of ARO-APOC3 in Healthy Volunteers, Hypertriglyceridemic Patients and Patients With Familial Chylomicronemia Syndrome (FCS)

A Phase 1 Single and Multiple Dose-Escalating Study to Evaluate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamic Effects of ARO-APOC3 in Adult Healthy Volunteers as Well as in Severely Hypertriglyceridemic Patients and Patients With Familial Chylomicronemia Syndrome

Status
Completed
Phase
Phase 1
Study type
Interventional
Enrollment
112 (actual)
Sponsor
Arrowhead Pharmaceuticals · Industry
Sex
All
Age
18 Years – 70 Years
Healthy volunteers
Accepted

Summary

The purpose of this study is to evaluate the safety, tolerability, pharmacokinetics and pharmacodynamics of single- and multiple doses of ARO-APOC3 in healthy adult volunteers and in patients with severe hypertriglyceridemia and familial chylomicronemia syndrome (FCS).

Conditions

Interventions

TypeNameDescription
DRUGARO-APOC3single or multiple doses of ARO-APOC3 by subcutaneous (sc) injections
DRUGsterile normal saline (0.9% NaCl)calculated volume to match active treatment

Timeline

Start date
2019-03-08
Primary completion
2021-02-11
Completion
2021-02-11
First posted
2018-12-21
Last updated
2025-12-24

Locations

10 sites across 3 countries: Australia, Canada, New Zealand

Regulatory

Source: ClinicalTrials.gov record NCT03783377. Inclusion in this directory is not an endorsement.