Trials / Unknown
UnknownNCT03588078
Study of the Safety and Efficacy of APR-246 in Combination With Azacitidine
A Phase 1b/2 Study to Evaluate the Safety and Efficacy of APR-246 in Combination With Azacitidine for the Treatment of Mutation TP53 (TP53) Mutant Myeloid Neoplasms
- Status
- Unknown
- Phase
- Phase 1 / Phase 2
- Study type
- Interventional
- Enrollment
- 53 (actual)
- Sponsor
- Groupe Francophone des Myelodysplasies · Academic / Other
- Sex
- All
- Age
- 18 Years
- Healthy volunteers
- Not accepted
Summary
The main purpose of this study is to determine the safe and efficacy of APR-246 in combination with azacitidine as well as to see complete remission of this patients
Detailed description
Patients will be treated for a total of 6 cycles.For patients responding or who have stable disease following cycle 6, treatment may continue until one of the following criteria applies: * Inter-current illness that prevent further administration of treatment * Unacceptable adverse event(s) * Participant decides to withdraw from the study, * general or specific changes in the participant's condition render the participant unacceptable for further treatment in the judgment of the investigator. * Evidence of disease progression by international working Group (IWG) 2006 criteria. * participants who wish not to continue treatment at time of disease assessment at end of cycle 6 will complete their end of treatment visit upon completion of cycle 6
Conditions
- Myelodysplastic Syndrome With Gene Mutation
- Acute Myeloid Leukemia With Gene Mutations
- Myeloproliferative Neoplasm
- Chronic Myelomonocytic Leukemia
Interventions
| Type | Name | Description |
|---|---|---|
| DRUG | APR-246 | Azacitidine at maximum tolerated dose. APR246 at the Dose limited Toxicity (DLT) dose |
| DRUG | Azacitidine | azacitidine is administered subcutaneously (SC) or via IV at 75 mg/m2 |
Timeline
- Start date
- 2018-09-15
- Primary completion
- 2020-05-01
- Completion
- 2021-05-15
- First posted
- 2018-07-17
- Last updated
- 2020-01-30
Locations
7 sites across 1 country: France
Regulatory
- FDA-regulated drug study
Source: ClinicalTrials.gov record NCT03588078. Inclusion in this directory is not an endorsement.