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Active Not RecruitingNCT03531255

Pegcetacoplan Long Term Safety and Efficacy Extension Study

An Open Label, Non-Randomized, Multi-Center Extension Study to Evaluate the Long-Term Safety and Efficacy of Pegcetacoplan in the Treatment of Paroxysmal Nocturnal Hemoglobinuria (PNH)

Status
Active Not Recruiting
Phase
Phase 3
Study type
Interventional
Enrollment
160 (estimated)
Sponsor
Apellis Pharmaceuticals, Inc. · Industry
Sex
All
Age
18 Years
Healthy volunteers
Not accepted

Summary

This is an Open-label, Non-Randomized, Multi-Center Extension Study. Eligible subjects will have previously completed a pegcetacoplan study.

Conditions

Interventions

TypeNameDescription
DRUGPegcetacoplanComplement (C3) Inhibitor

Timeline

Start date
2018-08-27
Primary completion
2025-11-29
Completion
2026-07-01
First posted
2018-05-21
Last updated
2026-04-06

Locations

62 sites across 21 countries: United States, Australia, Belgium, Bulgaria, Canada, Colombia, France, Germany, Hong Kong, Japan, Malaysia, Mexico, Peru, Philippines, Russia, Serbia, Singapore, South Korea, Spain, Thailand, United Kingdom

Regulatory

Source: ClinicalTrials.gov record NCT03531255. Inclusion in this directory is not an endorsement.

Pegcetacoplan Long Term Safety and Efficacy Extension Study (NCT03531255) · Clinical Trials Directory