Trials / Completed
CompletedNCT03398824
Pilot Study of Metformin for Patients With Fanconi Anemia
- Status
- Completed
- Phase
- Phase 2
- Study type
- Interventional
- Enrollment
- 15 (actual)
- Sponsor
- Boston Children's Hospital · Academic / Other
- Sex
- All
- Age
- 6 Years – 35 Years
- Healthy volunteers
- Not accepted
Summary
This is a single institution, open-label, single arm pilot study of Metformin in patients with Fanconi Anemia (FA) and cytopenias with the primary endpoint of hematologic response. This study will also assess safety, tolerability, and the biologic effects of Metformin in patients with FA.
Conditions
Interventions
| Type | Name | Description |
|---|---|---|
| DRUG | metformin HCl | Receive metformin HCl |
Timeline
- Start date
- 2018-03-29
- Primary completion
- 2020-10-09
- Completion
- 2020-10-09
- First posted
- 2018-01-16
- Last updated
- 2022-11-29
- Results posted
- 2022-11-29
Locations
1 site across 1 country: United States
Regulatory
- FDA-regulated drug study
Source: ClinicalTrials.gov record NCT03398824. Inclusion in this directory is not an endorsement.