Trials / Unknown
UnknownNCT03278899
A Study to Prospectively Assess Disease Progression in Male Children With X-ALD
A Non-interventional Study to Prospectively Assess Baseline Status and Disease Progression in Male Children With X-Linked Adrenoleukodystrophy
- Status
- Unknown
- Phase
- —
- Study type
- Observational
- Enrollment
- 100 (estimated)
- Sponsor
- NeuroVia, Inc. · Industry
- Sex
- Male
- Age
- 2 Years – 13 Years
- Healthy volunteers
- Not accepted
Summary
This is a non-interventional, multi-center study that follows general principles of periodic assessment of X-ALD patients in routine practice. No study drug treatment will be given and no changes to patient treatment are necessary.
Detailed description
This is a non-interventional, multi-center study that follows general principles of periodic assessment of X-ALD patients in routine practice. No study drug treatment will be given and no changes to the patient treatment are necessary. Patients with X-ALD will be recruited and invited to attend a baseline visit. After eligible patients are enrolled, retrospective and baseline data will be collected. After enrollment, patients will be seen approximately every 6 months until they meet withdrawal criteria or the Sponsor terminates the study.
Conditions
Timeline
- Start date
- 2018-02-16
- Primary completion
- 2021-06-01
- Completion
- 2021-06-01
- First posted
- 2017-09-12
- Last updated
- 2018-08-08
Locations
3 sites across 1 country: United States
Source: ClinicalTrials.gov record NCT03278899. Inclusion in this directory is not an endorsement.