Trials / Unknown
UnknownNCT03227042
A Prospective Natural History Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)
- Status
- Unknown
- Phase
- —
- Study type
- Observational
- Enrollment
- 44 (actual)
- Sponsor
- Allievex Corporation · Industry
- Sex
- All
- Age
- 18 Years
- Healthy volunteers
- Not accepted
Summary
This is a natural history study for children up to 18 years of age who have been diagnosed with Mucopolysaccharidosis Type IIIB (MPS IIIB, also known as Sanfilippo Syndrome Type B). Mucopolysaccharidosis type IIIB is a severe neurodegenerative disorder. The information gathered from this trial may help inform the design and interpretation of subsequent interventional studies. No clinical intervention or study drug is provided by Allievex in this study.
Conditions
Timeline
- Start date
- 2017-11-16
- Primary completion
- 2025-10-01
- Completion
- 2025-12-01
- First posted
- 2017-07-24
- Last updated
- 2022-10-26
Locations
9 sites across 9 countries: United States, Argentina, Australia, Brazil, Colombia, Germany, Spain, Taiwan, Turkey (Türkiye)
Source: ClinicalTrials.gov record NCT03227042. Inclusion in this directory is not an endorsement.